New method makes transgene-free gene editing even more promising

Genetically modified organisms, also known as GMOs, have been a hot topic of conversation among researchers, producers, ...
Science Daily

Scientists just made gene editing far more powerful

Scientists at The University of Texas at Austin have developed a revolutionary gene-editing method using bacterial retrons ...
abc27

Ajinomoto Bio-Pharma Services and Gene Tools Announce Collaboration to Expand Access to PMO Therapeutics

TOKYO, Oct. 21, 2025 /PRNewswire/ -- Ajinomoto Bio-Pharma Services ("Aji Bio-Pharma"), a leading provider of biopharmaceutical contract development and manufacturing services, and Gene Tools, LLC ...
The Bakersfield Californian

Landmark Bio Forges New Collaboration to Accelerate Early-Stage Translational Cell and Gene Therapies

Landmark Bio, LLC today announced the initiation of a new collaboration with Mass General Brigham to provide development and manufacturing services for cell and gene therapies originating from the ...
The New England Journal of Medicine

Long-Term Safety and Efficacy of Gene Therapy for Adenosine Deaminase Deficiency

These long-term findings in a large patient cohort show the sustained clinical efficacy and safety of autologous CD34+ hematopoietic stem-cell lentiviral gene therapy for ADA-SCID, indicating that it ...
STAT

Sarepta to seek approval for gene therapy in rare form of muscular dystrophy

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...
Hosted on MSN

'Match Game on tonight: Who is Martin Short dating? When does ‘Only Murders’ return?

Martin Short has spent 50 years in the spotlight, but "game show host" was never among his many accolades until now, when he serves as ringleader tonight, July 23, for ABC's "Match Game" revival.
FierceBiotech

Chiesi fertilizes Arbor's rare disease gene therapy efforts with $2B biobucks deal

A few months after launching its lead gene therapy into the clinic, Arbor Biotechnologies has found a European partner to come along for the ride. Italian pharma Chiesi is fertilizing Arbor’s rare ...
BioWorld

Arbor Bio in $2B+ deal with Chiesi for gene editing therapies

In a deal that could bring more than $2.1 billion in payments to Arbor Biotechnologies Inc., 90-year-old Chiesi Group gained exclusive and global rights to develop and commercialize ABO-101 for ...
MedPage Today

First Child Dosed in Gene Therapy Trial Dies

The first participant in an investigational gene therapy trial of STXBP1 encephalopathy died, Capsida Biotherapeutics said. The death occurred days after dosing, according to information posted on the ...
ABC News

Preliminary but promising gene therapy shows 75% reduction in Huntington's disease progression

Scientists report the first therapy to slow the deadly brain disease. A one-time gene therapy treatment has shown remarkable success in slowing the progression of Huntington's disease in a preliminary ...