Genetic disorders occur due to alterations in the primary genetic material—deoxyribonucleic acid (DNA)—of an organism.

Humanized mouse models are vital for studying human gene function, but fully replacing mouse genes with complete human ...

CRISPR–Cas9-based therapies are widely investigated for their clinical applications. However, there are limitations ...

Scientists and physicians can better assess precision genome editing technology using a new method made public today by St.

Scientists first read the human genome, a three-billion-letter biological book, in April 2003. Since then, researchers have steadily advanced the ability to write DNA, moving far beyond single-gene ...

Understanding human gene function in living organisms has long been hampered by fundamental differences between species. Although mice share most ...

GenEditBio Limited ("GenEditBio"), a clinical-stage biotechnology startup focusing on genome-editing therapeutic solutions, ...

The clearance allows human trials for its one-time treatment targeting a genetic eye disease that causes vision loss.

Genetic disorders occur due to alterations in the primary genetic material, deoxyribonucleic acid (DNA), of an organism.

Aurora Therapeutics, cofounded by Nobel Prize–winning scientist Jennifer Doudna, plans to use gene editing and a new FDA ...