In an important new study, Chinese researchers have discovered the previously unrecognized role of alternative splicing of ...

In a new study, Chinese researchers have discovered the previously unrecognized role of alternative splicing of the DOC2A ...

British scientists have made a potentially important discovery related to dementia and Alzheimer’s disease that could pave ...

The first patient has been dosed in a Phase 2 clinical trial testing RAG-17 in people with ALS who carry mutations in the ...

Professor Peng Donghai of Huazhong Agricultural University in Wuhan, Hubei province, has received a top award in recognition ...

Maze Therapeutics uses its Compass genetics platform to advance kidney and obesity drugs, with MZE829 Phase 2 data due in ...

Ocugen’s AAV gene therapy, OCU410, has demonstrated its capacity to reduce geographic atrophy (GA)-associated lesion growth in the Phase II ArMaDa trial. Image credit: VectorsMarket via ...

University of Utah researchers at the Pulst-Scoles Laboratory have discovered that reducing levels of the STAUFEN-1 protein ...

A new mouse study suggests that "beige" fat surrounding blood vessels can send calming signals to the arteries—revealing an ...

A new LUMC study has changed our understanding of how cells work. Researchers have discovered that the CFAP20 protein acts as ...

Stoke Therapeutics advances TANGO ASO for Dravet, with Zorevunersen Phase 3 data showing seizure reduction and a delayed 2027 ...

AAVantgarde Bio (AAVantgarde), a clinical-stage biotechnology company pioneering therapies for inherited retinal diseases (IRDs), has announced the completion of enrollment in LUCE-1, their Phase 1/2 ...