Two complementary studies led by researchers from the Yong Loo Lin School of Medicine, National University of Singapore (NUS ...

The small interfering RNA (siRNA) therapy, designed to reduce triglyceride levels by suppressing production of apolipoprotein ...

Ionis is planning a supplemental submission by the end of the year to expand Tryngolza into severe hypertriglyceridemia. If ...

Scientists at St. Jude Children's Research Hospital and Northwestern University identified a previously unknown treatment ...

Aperture Therapeutics, a biotechnology company pioneering next-generation precision medicines for neurodegenerative diseases, today announced the nomination of APRTX-001 as its development candidate.

Researchers in Singapore have developed a dual RNA therapy that silences mutant KRAS and activates immune signalling, ...

NUS Medicine-led study shows extracellular vesicles carrying gene-targeting antisense oligonucleotides (ASOs) and immune ...

As China's healthcare and policy environment continues to improve, global pharmaceutical company GlaxoSmithKline (GSK) is ...

Transposable elements play a significant role in regulating gene expression and genome architecture, influencing development, ...

NOVATO, Calif., Oct. 30, 2025 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE) today announced that the first patient has been dosed in the Aurora study (NCT07157254) evaluating the ...

The presentation featured pooled 48-week data from two multicenter, randomized Phase II studies (Phase IIa, NCT06115993; Phase IIb, NCT06550128) in HBeAg-negative chronic hepatitis B (CHB) patients ...

Sana Biotechnology, CAMP4 Therapeutics and Crinetics Pharmaceuticals have all used the third quarter to refocus their ...