Two complementary studies led by researchers from the Yong Loo Lin School of Medicine, National University of Singapore (NUS ...

The small interfering RNA (siRNA) therapy, designed to reduce triglyceride levels by suppressing production of apolipoprotein ...

Aperture Therapeutics, a biotechnology company pioneering next-generation precision medicines for neurodegenerative diseases, today announced the nomination of APRTX-001 as its development candidate.

Researchers in Singapore have developed a dual RNA therapy that silences mutant KRAS and activates immune signalling, ...

NUS Medicine-led study shows extracellular vesicles carrying gene-targeting antisense oligonucleotides (ASOs) and immune ...

A study has confirmed the effectiveness of a drug that can treat acquired genetic hearing loss. On the 11th, a research team led by Professor Ji Heon-young, Professor Jang Seung-hyun of Yonsei ...

There was an increase in the hepatic fat fraction, the long-term consequences of which are unknown, says Robert Rosenson.

GATC brought together a broad coalition of researchers and executives in cell and gene therapy, gene editing, drug discovery and AI as well as patients and advocates.

The FDA’s Marty Makary and Vinay Prasad have laid out a path for CRISPR treatments on demand. An expert weighs in on what it ...

Quality, stability, sustainability, and the increased and thoughtful integration of artificial intelligence are foremost in the minds of those on the leading edge of testing trends.

Researchers have found a new way to reactivate fetal hemoglobin without the need for gene-editing therapy, according to a new study.

They face a difficult choice, since the treatment may benefit their children but comes with serious risks and unknowns, particularly following reports of patient deaths.