The FDA granted fast track status to VectorY’s VTx-002, an antibody gene therapy targeting TDP-43 protein aggregates in ALS.

Mutations in the tumor suppressor TP53 are a common cause of cancer, making the altered protein an attractive target for ...

Precision and timing of gene expression is essential for normal biological functions and, when disrupted, can lead to many ...

In a groundbreaking study published in the in Proceedings of the National Academy of Sciences (PNAS), scientists at Pacific ...

More than 9 out of 10 Alzheimer's cases could be driven by specific variations in a single gene and the protein it produces, ...

We know the genes, but not their functions—to resolve this long-standing bottleneck in microbial research, a joint research ...

The small study in patients with a rare disorder that causes liver and lung damage showed the potential for precisely targeted infusions. By Gina Kolata Researchers have corrected a disease-causing ...

Not only have researchers identified how a common cellular protein affects aging, but they’ve tweaked the genes that produce it in fruit flies, extending healthy lifespan by 25% to 30%. The discovery ...